The development of a brain tumor in a study participant led regulators to suspend a Hurler syndrome therapy in early testing ...

The discovery of a tumor in a patient who received REGENXBIO’s gene therapy for Hurler syndrome prompted the FDA to place a hold on that program along with the company’s Hunter syndrome program, which ...

Immusoft of CA, a clinical-stage biotechnology company pioneering engineered B cell therapies, today announced that the U.S. Food and Drug Administration (FDA) has granted Rare Pediatric Disease (RPD) ...

Turns out Black got a bit too big for his britches requesting a rewrite, which ultimately got his Pixar offer revoked. Reading time 2 minutes No one would argue that Jack Black is an actor so ...

Preparing for FDA approval and commercial launch of tividenofusp alfa, Denali’s TransportVehicle™ (TV)-enabled investigational therapy for Hunter syndrome Expecting multiple clinical data readouts ...

STATEN ISLAND, N.Y. — New York City residents are living longer than ever before, but longstanding demographic disparities have persisted across the five boroughs. On Tuesday, the city Health ...

The 2022 Bexar County community health needs assessment revealed a painful truth: Where you live in San Antonio has a powerful influence on your health and your life expectancy. The report found that ...

Background: Cardiovascular Disease (CVD) represents a significant global public health challenge. Metabolic Syndrome (MetS) notably elevates the risk of CVD, with MetS patients facing approximately ...

Mucopolysaccharidosis II is currently treated with an enzyme replacement therapy that does not cross the blood-brain barrier and thus does not address the condition's neurologic consequences. This ...