U.S. health officials have added two deadly rare diseases to the list of conditions the government recommends states screen ...
U.S. Health Secretary Robert F. Kennedy Jr. on Tuesday added two rare genetic disorders, Duchenne Muscular Dystrophy and ...
Gene editing has the potential to cure thousands of people suffering from devastating rare diseases. But the Nobel ...
Backed by a handful of prominent investors including the Gates Foundation, the startup is pursuing an approach it believes ...
The nonprofit is funding research at two universities—Oregon Health & Science University and UMass Chan Medical School—on a ...
Once seen as a last resort, bone marrow transplantation is now being viewed as a potential cure for several rare blood ...
Ohio State student Cailin Joyce died after suffering a rare blood disorder caused by the Epstein-Barr virus that “left her ...
The FDA has granted approval to a new gene therapy for a rare immune disorder, the maker of which is notably not a drug ...
The donation from Don and Anne Edwards aims to speed research, treatment and diagnosis for children with rare and genetic ...
Addition joins a growing list of launches this year, following in the footsteps of startups like Crystalys Therapeutics and ...
The Covid-19 pandemic brought rare disease research to a standstill. Five years later, patients and advocates say the ...
Soleo Health has appointed Jody Thompson as senior vice president of business development, rare disease, to broaden the company’s portfolio of exclusive and limited distribution therapies for rare, ...
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