For generations, Sickle Cell Disease has been a devastating illness affecting millions of people around the world, ...

Genetic defects are exceedingly common, which is not surprising considering just how many cells make up our bodies, including our reproductive cells. While most of these defects have no or only minor ...

People with a rare genetic disorder that damages the amygdala are helping neuroscientists rethink how the brain shapes fear, ...

A University of Texas at Austin-led team has reconstructed the most detailed map to date of the molecular machines that ...

A UCSF team has submitted an application to the FDA seeking approval for a small trial of in utero gene therapy for a rare ...

A new study has uncovered a genetic cause that may explain why some people develop Kaposi sarcoma despite having no apparent ...

Novel CRISPR-Cas9 treatments are proving effective in reversing disease for life. But ensuring their long-term safety will ...

Please provide your email address to receive an email when new articles are posted on . The expression of GSDMB was high in children with a 17q21 genetic variant. These children did not have ...

Myotonic dystrophy is thought to be caused by the binding of a protein called Mbnl1 to abnormal RNA repeats. In these two images of the same muscle precursor cell, the top image shows the location of ...

Opus Genetics (NASDAQ:IRD) is advancing a portfolio of gene therapies for inherited retinal diseases, with two programs ...