With the FDA expecting to approve 10–20 Cell and Gene Therapies (CGTs) annually by 2025, it is evident that the field will continue to hold immense commercial and medical opportunities. To harness ...
Gene therapy is reshaping modern medicine, offering the potential for lasting, even curative treatments for a wide range of ...
There is no margin for error in the pharma and biopharma sectors. If the chain-identity breaks anywhere along the way, there ...
This story is part of a series on the current progression in Regenerative Medicine. In 1999, I defined regenerative medicine as the collection of interventions that restore tissues and organs damaged ...
The recent approval of Regeneron’s Otarmeni underscores the maturation of gene therapies across a range of diseases. Here, ...
Beta thalassemia major, also known as Cooley’s anemia and transfusion-dependent beta thalassemia, causes the body’s red blood ...
BUFFALO, N.Y. — A viral gene therapy developed by University at Buffalo researchers has reversed some brain abnormalities in infant mice with FOXG1 syndrome, a significant step toward one day treating ...
INDIANAPOLIS – Elin Lewis, a 12-year-old from Greenwood, has made history as the first patient in the state to receive a ...
What Is Kresladi, and Why Does It Matter? Kresladi (marnetegragene autotemcel) is a gene therapy approved by the FDA to treat a rare and serious immune condition called leukocyte adhesion deficiency ...
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